The investigational treatment BPN14770 improved language skills, cognition, and caregiver-assessed daily functioning ability in adults with fragile X syndrome,…
Articles by Marisa Wexler, MS
A majority of rare disease patients using telehealth during the COVID-19 pandemic thought the experience positive, and many would like…
Zygel, an experimental cannabidiol (CBD) gel, may lessen the extent of behavioral abnormalities in children with…
The National Institutes of Health (NIH) is awarding multi-year grants to three centers conducting collaborative research into fragile…
Clinical improvements among participants receiving a placebo — known as the placebo effect — are common in clinical trials…
The experimental cannabidiol (CBD) gel Zygel eased behavioral problems in children with fragile X syndrome and benefited those with…
The common type 2 diabetes medication metformin eased the excessive production of proteins in nerve cells that were engineered in…
Zynerba Pharmaceuticals‘ Zygel failed to significantly ease behavioral symptoms in the overall group of children with…
Top-line results from the CONNECT-FX trial testing the cannabidiol (CBD) gel Zygel as a potential treatment for behavioral…
A procedure for measuring language skills, called expressive language sampling (ELS), could be used to assess treatment outcomes in people…